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Spinraza Access and Sites

We will continue to update our community on administration sites, insurance coverage, and community resources and support programs for Spinraza.

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Conference Conference Conference

2018 Annual SMA Conference

Registration is now open for the 2018 Annual SMA Conference, scheduled for June 14 -17, 2018 at the Hilton Anatole Hotel in Dallas, TX!

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Events Events Events

Fall Events

Fall event season is in full swing. Join us! Find an upcoming event in your area, or host your own event.

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Cure SMA Meets in Utah with State and Federal Elected Officials to Support Newborn Screening

Cure SMA Meets in Utah with State and Federal Elected Officials to Support Newborn Screening

On Tuesday, Cure SMA staff members and family advocates, and clinicians from the University of Utah, met with Senator Orrin Hatch (R-UT) to...

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Genentech/Roche Releases Clinical Trial Update for SUNFISH (RG7916)

Genentech/Roche Releases Clinical Trial Update for SUNFISH (RG7916)

Genentech/Roche has provided the below community statement with clinical trial updates for SUNFISH (Type 2/3). The first patient is now enrolled...

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2017 SMA Awareness Month Recap

2017 SMA Awareness Month Recap

The SMA community celebrated an impactful and advocacy-driven Awareness Month through a number of ways this August. Whether hosting candlelight...

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Recording of the September Webinar on Spinraza Updates Now Available

A recording of last week’s webinar updating the...

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AveXis Announces Plan to Initiate Pivotal Trial of AVXS-101 in SMA Type 1 Using Product from New GMP Commercial Process

AveXis Announces Plan to Initiate Pivotal Trial of AVXS-101 in SMA Type 1 Using Product from New GMP Commercial Process

AveXis, Inc., a clinical-stage gene therapy company developing treatments for patients suffering from rare and life-threatening neurological...

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