News

October 8, 2018

New Spinraza Data Presented at Annual Congress of the World Muscle Society Demonstrate Benefits in Treating Presymptomatic Infants with SMA

New Spinraza Data Presented at Annual Congress of the World Muscle Society Demonstrate Benefits in Treating Presymptomatic Infants with SMA

Biogen, Inc. announced new interim results from NURTURE, an ongoing open-label, single-arm efficacy and safety study of SPINRAZA® (nusinersen) in 25...

READ MORE   |  

Topics: Clinical Trials, Research, Front Page News

October 5, 2018

Cytokinetics and Astellas Provide Clinical Trial Updates for Reldesemtiv in SMA

Cytokinetics and Astellas Provide Clinical Trial Updates for Reldesemtiv in SMA

Cytokinetics, Incorporated and Astellas Pharma Inc. today provided an update for their collaborative skeletal muscle program, including clinical trial updates for reldesemtiv in SMA.

In June, Cytokinetics announced data from a Phase...

READ MORE   |  

Topics: Clinical Trials, Research, Front Page News

October 3, 2018

Genentech Announces New Data for Risdiplam in Spinal Muscular Atrophy (SMA) at the World Muscle Society Congress

Genentech Announces New Data for Risdiplam in Spinal Muscular Atrophy (SMA) at the World Muscle Society Congress

Genentech, a member of the Roche Group (SIX: RO, ROG; OTCQX: RHHBY), announced today interim clinical data from the dose-finding parts of the pivotal FIREFISH and...

READ MORE   |  

Topics: Clinical Trials, Research, Front Page News

October 3, 2018

Genentech Releases Community Statement on Risdiplam

Genentech Releases Community Statement on Risdiplam

The following statement is a community update from Genentech/Roche on the risdiplam studies FIREFISH and SUNFISH. 

Dear SMA community,

We are happy to share an update on our FIREFISH and SUNFISH studies of risdiplam. We would also like to acknowledge the tremendous support...

READ MORE   |  

Topics: Clinical Trials, Research, Front Page News

September 12, 2018

Cure SMA's Approach to Newborn Screening

Cure SMA's Approach to Newborn Screening

The complexities of newborn screening require a sophisticated, multifaceted approach. With this in mind, Cure SMA has been working on newborn screening through several different avenues, bringing our full resources to ensure that babies born with SMA have the opportunity to receive early...

READ MORE   |  

Topics: Support & Care, Advocacy, Research, Front Page News

August 28, 2018

Cure SMA Provides Funding for "Patient Reported Impact of Symptoms in Spinal Muscular Atrophy (PRISM-SMA)" Published in Neurology

Cure SMA Provides Funding for

In a recent paper titled, “Patient Reported Impact of Symptoms in Spinal Muscular Atrophy (PRISM-SMA)” Dr. Chad Heatwole and others describe a cross-sectional study of 359 adults with SMA using the International SMA Patient Registry. The goal of the study was to determine the...

READ MORE   |  

Topics: Our Impact, Research, Front Page News

August 17, 2018

Cure SMA Provides Funding and Recruitment for the NeuroNEXT SMA Biomarker Study: Super Babies for SMA!

Cure SMA Provides Funding and Recruitment for the NeuroNEXT SMA Biomarker Study: Super Babies for SMA!

A recent paper published in the Journal of Contemporary Clinical Trials Communications titled, “Recruitment & retention program for the NeuroNEXT SMA Biomarker Study: Super Babies for...

READ MORE   |  

Topics: Our Impact, Research, Front Page News

August 16, 2018

Updated 2018 SMA Standards of Care Statements Available Online

The 2018 SMA Standards of Care recommendations were published in Neuromuscular Disorders in February 2018 and March 2018 and are available online through Open Access for families and healthcare providers. These documents are updates of the Standard of Care document issued in 2007.

The 2018 recommendations emphasize that "a...

READ MORE   |  

Topics: Support & Care, Research, Front Page News

August 3, 2018

2018 SMA Researcher Meeting Summary: SMA Therapy Development

2018 SMA Researcher Meeting Summary: SMA Therapy Development

The SMA Researcher Meeting is the largest research meeting in the world specifically focused on SMA and seeks to create open communication of early, unpublished data to accelerate the pace of research. The meeting also furthers...

READ MORE   |  

Topics: Conference, Research, Front Page News

July 27, 2018

2018 SMA Researcher Meeting Summary: Clinical Research Studies for SMA

2018 SMA Researcher Meeting Summary: Clinical Research Studies for SMA

The SMA Researcher Meeting is the largest research meeting in the world specifically focused on SMA and seeks to create open communication of early, unpublished data to accelerate the pace of research. The meeting also furthers...

READ MORE   |  

Topics: Conference, Research, Front Page News

Items 1 - 10 of 228  12345678910Next

© 2018 Cure SMA | Privacy Policy

Powered by Blackbaud
nonprofit software