News

April 18, 2018

Spring 2018 Issue of Compass Now Available Online

Spring 2018 Issue of Compass Now Available Online

The Spring 2018 issue of Compass is now available online. The issue covers Cure SMA’s newborn screening efforts, including how NBS can help children diagnosed with SMA, the addition of SMA to the federal Recommended...

READ MORE   |  

Topics: Research, Advocacy, Front Page News

April 16, 2018

Genentech to Present New RG7916 Data at the American Academy of Neurology (AAN) Annual Meeting

Genentech to Present New RG7916 Data at the American Academy of Neurology (AAN) Annual Meeting

Genentech/Roche announced today that new data on its approved and investigational medicines for neurological conditions will be presented during the 70th American Academy of Neurology (AAN) Annual Meeting from April 21-27 in Los Angeles, California. The data will include investigational...

READ MORE   |  

Topics: Clinical Trials, Research, Front Page News

April 13, 2018

Cure SMA Awards $150,000 Grant to Bakri Elsheikh, MD, Ohio State University Wexner Medical Center

Cure SMA Awards $150,000 Grant to Bakri Elsheikh, MD, Ohio State University Wexner Medical Center

Cure SMA has awarded a $150,000 research grant to Bakri Elsheikh, MD, at the Ohio State University Wexner Medical Center, for his project, "Determine the motor unit response following SMN restoration in late-onset spinal muscular atrophy”.

Dr. Elsheikh and his team will study...

READ MORE   |  

Topics: Our Impact, Research, Front Page News

April 9, 2018

Cure SMA Database Findings Published in the Journal of Neuromusular Diseases

Cure SMA Database Findings Published in the Journal of Neuromusular Diseases

An important goal at Cure SMA is to collect data to better understand the SMA patient population, and then to report this data back to our industry partners, regulators, and payers. In collecting this data, we also hope to identify areas where additional care, advocacy, support, and research...

READ MORE   |  

Topics: Our Impact, Research, Front Page News

April 9, 2018

Novartis Agrees to Acquire AveXis

Novartis Agrees to Acquire AveXis

AveXis, Inc. and Novartis announced today that they have entered into an agreement and plan of merger. Novartis will acquire AveXis in a transaction unanimously approved by the Boards of Directors of both companies.

Novartis plans a smooth transition of AveXis operations and the...

READ MORE   |  

Topics: Research, Front Page News

April 6, 2018

The Genetics of SMA – What is the SMN1 Gene?

The Genetics of SMA – What is the SMN1 Gene?

Spinal muscular atrophy is caused when an individual has two missing or faulty SMN1 genes. But what is the SMN1 gene, and what does it do?

About the SMN1 Gene

SMN1 stands for survival motor gene 1. This gene is responsible for...

READ MORE   |  

Topics: About SMA, Research, Front Page News

March 29, 2018

Cure SMA Awards $150,000 Grant to Brunhilde Wirth, PhD, Institute of Cologne, Germany

Cure SMA Awards $150,000 Grant to Brunhilde Wirth, PhD, Institute of Cologne, Germany

Cure SMA has awarded a $150,000 research grant to Brunhilde Wirth, PhD, at Institute of Cologne, Germany, for her project, "Study of combinatorial therapy based on SPINRAZA together with a novel protective genetic modifier.”

Based on so-called SMA discordant families, in whom...

READ MORE   |  

Topics: Our Impact, Research, Front Page News

March 29, 2018

Cure SMA Awards $50,000 Grant to Rashmi Kothary, PhD, University of Ottawa

Cure SMA Awards $50,000 Grant to Rashmi Kothary, PhD, University of Ottawa

Cure SMA has awarded a $50,000 research grant to Rashmi Kothary, PhD, at the University of Ottawa, for his project, " The shifting landscape of SMA research: towards a better understanding for a role for SMN in aging.”

In this proposal, Dr. Kothary and his team seek to explore...

READ MORE   |  

Topics: Our Impact, Research, Front Page News

March 29, 2018

Scholar Rock Granted Orphan Drug Designation by the FDA for SRK-015 for the Treatment of Patients with SMA

Scholar Rock Granted Orphan Drug Designation by the FDA for SRK-015 for the Treatment of Patients with SMA

Scholar Rock today announced that the U.S. Food and Drug Administration (FDA) has granted Orphan Drug...

READ MORE   |  

Topics: Clinical Trials, Research, Front Page News

March 28, 2018

Cure SMA Awards $150,000 Grant to Robin Parks, PhD, University of Ottawa

Cure SMA Awards $150,000 Grant to Robin Parks, PhD, University of Ottawa

Cure SMA has awarded a $150,000 research grant to Robin Parks, PhD, at the University of Ottawa, for his project, "Serum-derived exosomes as a biomarker for Spinal Muscular Atrophy.”

Dr. Parks and his team are exploring the use of exosomes, small particles released from all...

READ MORE   |  

Topics: Our Impact, Research, Front Page News

Items 1 - 10 of 197  12345678910Next

© 2018 Cure SMA | Privacy Policy

Powered by Blackbaud
nonprofit software