September 19, 2017
Novartis has released the following update for the LMI070 (branaplam) clinical trial, on behalf of the program team.
Dear SMA community,
For years, our researchers have been working hard to develop a new treatment for SMA. One promising compound in our neuroscience...
September 18, 2017
Cure SMA is expanding its role in spinal muscular atrophy medical affairs at the national level through its Medical Advisory Council (MAC). The MAC sets the agenda for proactive, creative, and collaborative leadership on issues that improve the quality of medical care for those affected by SMA.
The focus of the Council is to build on...
September 15, 2017
Genentech/Roche recently provided the following community statement with clinical trial updates for SUNFISH (Type 2/3). The SUNFISH trial is advancing to part two, which is designed to be a pivotal, marketing registration trial.
Dear SMA Community,
We are focused on...