News

March 29, 2018

Cure SMA Awards $50,000 Grant to Rashmi Kothary, PhD, University of Ottawa

Cure SMA Awards $50,000 Grant to Rashmi Kothary, PhD, University of Ottawa

Cure SMA has awarded a $50,000 research grant to Rashmi Kothary, PhD, at the University of Ottawa, for his project, " The shifting landscape of SMA research: towards a better understanding for a role for SMN in aging.”

In this proposal, Dr. Kothary and his team seek to explore...

READ MORE   |  

Topics: Our Impact, Research, Front Page News

March 29, 2018

Scholar Rock Granted Orphan Drug Designation by the FDA for SRK-015 for the Treatment of Patients with SMA

Scholar Rock Granted Orphan Drug Designation by the FDA for SRK-015 for the Treatment of Patients with SMA

Scholar Rock today announced that the U.S. Food and Drug Administration (FDA) has granted Orphan Drug...

READ MORE   |  

Topics: Clinical Trials, Research, Front Page News

March 28, 2018

Cure SMA Awards $150,000 Grant to Robin Parks, PhD, University of Ottawa

Cure SMA Awards $150,000 Grant to Robin Parks, PhD, University of Ottawa

Cure SMA has awarded a $150,000 research grant to Robin Parks, PhD, at the University of Ottawa, for his project, "Serum-derived exosomes as a biomarker for Spinal Muscular Atrophy.”

Dr. Parks and his team are exploring the use of exosomes, small particles released from all...

READ MORE   |  

Topics: Our Impact, Research, Front Page News

March 26, 2018

Cure SMA Welcomes Back Biogen as a National Premier Partner for 2018

Cure SMA Welcomes Back Biogen as a National Premier Partner for 2018

Cure SMA is thrilled to welcome Biogen back as a National Premier Partner for 2018.

As a part of their partnership, Biogen will be sponsoring all walk-n-rolls and galas across the US for the entirety of 2018, as well as the

READ MORE   |  

Topics: Support & Care, Events & Fundraising, Front Page News

March 23, 2018

House and Senate Vote to Increase Federal Funding for Newborn Screening Programs

House and Senate Vote to Increase Federal Funding for Newborn Screening Programs

Today, Congress passed a new federal spending bill, increasing funding for several critical newborn screening programs, that the President also signed. The bill increases funding for the Health Resources and Services Administration (HRSA) Heritable Disorders Program by more than $2...

READ MORE   |  

Topics: Support & Care, Advocacy, Front Page News

March 21, 2018

Cure SMA Awards $150,000 Grant to Charlotte Sumner, MD, Johns Hopkins University

Cure SMA Awards $150,000 Grant to Charlotte Sumner, MD, Johns Hopkins University

Cure SMA has awarded a $150,000 research grant to Charlotte Sumner, MD, at Johns Hopkins University, for her project, "Testing the potential of SMN-AS1 as a therapeutic target in SMA.”

Dr. Sumner and her team have recently identified a long noncoding RNA (lncRNA) that represses...

READ MORE   |  

Topics: About SMA, Research, Front Page News

March 20, 2018

Record Number of Abstracts Submitted for 2018 SMA Researcher Meeting

Abstract submission is now closed for the 2018 SMA Researcher Meeting. We are excited to announce that we received 128 submissions, a record number. Our submissions come from researchers in 16 countries, 11 companies, and close to 50 institutions.

We...

READ MORE   |  

Topics: Conference, Research, Front Page News

March 20, 2018

The Discovery of SMA

The Discovery of SMA

In 2016, the spinal muscular atrophy community celebrated the approval of the first-ever treatment that targets the underlying genetic cause of SMA. This was a milestone more than 100 years in the making, made possible by dedicated researchers, and the community that supported their...

READ MORE   |  

Topics: Community & Awareness, About SMA, Front Page News

March 15, 2018

Roche Releases Community Statement on RG7916 and Olesoxime Programs

Roche Releases Community Statement on RG7916 and Olesoxime Programs

Roche has provided the following community statement on RG7916 and Olesoxime investigational programs. 

Dear SMA Community, 

We are very pleased to share an update of the Roche SMA program We have two investigational molecules in development for people with SMA,...

READ MORE   |  

Topics: Clinical Trials, Research, Front Page News

March 14, 2018

Cure SMA Awards $75,000 Grant to Robert Kalb, MD, Northwestern University

Cure SMA Awards $75,000 Grant to Robert Kalb, MD, Northwestern University

Cure SMA has awarded a $75,000 research grant to Robert Kalb, MD, at Northwestern University Feinberg School of Medicine, for his project, "Effects of diminished SMN on segmental spinal cord innervation of motor neurons.”

Dr. Kalb and his team have conducted studies that indicate...

READ MORE   |  

Topics: Our Impact, Research, Front Page News

Items 61 - 70 of 516  Previous12345678910Next

© 2018 Cure SMA | Privacy Policy

Powered by Blackbaud
nonprofit software