March 29, 2018
Cure SMA has awarded a $50,000 research grant to Rashmi Kothary, PhD, at the University of Ottawa, for his project, " The shifting landscape of SMA research: towards a better understanding for a role for SMN in aging.”
In this proposal, Dr. Kothary and his team seek to explore...
March 28, 2018
Cure SMA has awarded a $150,000 research grant to Robin Parks, PhD, at the University of Ottawa, for his project, "Serum-derived exosomes as a biomarker for Spinal Muscular Atrophy.”
Dr. Parks and his team are exploring the use of exosomes, small particles released from all...
March 26, 2018
Cure SMA is thrilled to welcome Biogen back as a National Premier Partner for 2018.
As a part of their partnership, Biogen will be sponsoring all walk-n-rolls and galas across the US for the entirety of 2018, as well as the
March 23, 2018
Today, Congress passed a new federal spending bill, increasing funding for several critical newborn screening programs, that the President also signed. The bill increases funding for the Health Resources and Services Administration (HRSA) Heritable Disorders Program by more than $2...
March 21, 2018
Cure SMA has awarded a $150,000 research grant to Charlotte Sumner, MD, at Johns Hopkins University, for her project, "Testing the potential of SMN-AS1 as a therapeutic target in SMA.”
Dr. Sumner and her team have recently identified a long noncoding RNA (lncRNA) that represses...
March 20, 2018
Abstract submission is now closed for the 2018 SMA Researcher Meeting. We are excited to announce that we received 128 submissions, a record number. Our submissions come from researchers in 16 countries, 11 companies, and close to 50 institutions.
March 20, 2018
In 2016, the spinal muscular atrophy community celebrated the approval of the first-ever treatment that targets the underlying genetic cause of SMA. This was a milestone more than 100 years in the making, made possible by dedicated researchers, and the community that supported their...
March 15, 2018
Roche has provided the following community statement on RG7916 and Olesoxime investigational programs.
Dear SMA Community,
We are very pleased to share an update of the Roche SMA program We have two investigational molecules in development for people with SMA,...
March 14, 2018
Cure SMA has awarded a $75,000 research grant to Robert Kalb, MD, at Northwestern University Feinberg School of Medicine, for his project, "Effects of diminished SMN on segmental spinal cord innervation of motor neurons.”
Dr. Kalb and his team have conducted studies that indicate...