Cure SMA leads the way to a world where everyone impacted by spinal muscular atrophy is empowered to lead independent, successful, and fulfilling lives.

Our powerful progress includes:

  • Three approved treatments for SMA
  • Newborn screening across 100% of the U.S.
  • More clinical trials happening than ever before

However, our work is not over, and we need your support.

Spinal muscular atrophy (SMA) is a progressive neurodegenerative disease that affects the motor nerve cells in the spinal cord and impacts the muscles used for activities such as breathing, eating, crawling, and walking.

newly-diagnosed-icon

Newly Diagnosed

living-with-sma-icon

Living with
SMA

healthcare-provider-icon

Healthcare Provider

researcher-icon

Fundraising EventS

fundraiser-icon

Advocate

Cure SMA is committed to local support.
Find resources or treatment in your area.

Scroll to Top