Search Results: Evrysdi

Biogen Announces New Updates Across its SMA Research Program at 2023 MDA Conference

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First patient treated in the ASCEND study evaluating the potential benefit of investigational higher dose nusinersen in children, teens and adults previously treated with Evrysdi® (risdiplam) […]

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Cure SMA Awards $75,000 Grant to Lyndsay Murray, PhD, University of Edinburgh

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Lyndsay Murray, PhD, was awarded $75,000 for her research project, “Evaluating the impact of sequential versus simultaneous administration of SMN-inducing compounds on motor unit recovery […]

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Therapeutic Approaches

Make today a breakthrough. One of the strengths of Cure SMA’s drug discovery program is how we address spinal muscular atrophy (SMA) from multiple angles. […]

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Research Study Opportunities

Make today a breakthrough. By participating in a research study, you will help the scientific and research communities accelerate therapy development for spinal muscular atrophy […]

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FAQs & Glossary

Make today a breakthrough. Learn more about spinal muscular atrophy (SMA) by reading our frequently asked questions and glossary of common terms. If you still […]

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Newborn Screening for SMA

Make today a breakthrough. Evidence shows that early diagnosis through newborn screening and early intervention with available treatments lead to better outcomes. This is especially […]

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Find a Treatment Center

Make today a breakthrough. Our online location finder is designed to help individuals with spinal muscular atrophy (SMA) locate treatment and medical care in your […]

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Spinal Muscular Atrophy Treatment

Make today a breakthrough. There are several (SMA) spinal muscular atrophy treatments approved. Each individual or family must make treatment decisions based on your needs, […]

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SMA Awareness Month

SMA Awareness Month 2024 Coming Soon in August 2024   Spinal muscular atrophy (SMA) is a progressive neurodegenerative disease that affects the motor nerve cells […]

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Approaches to Drug Development

Make today a breakthrough. Due to a mutation in the survival motor neuron gene 1 (SMN1), individuals with spinal muscular atrophy (SMA) don’t produce survival […]

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