Search Results: Evrysdi

SMA Drug Pipeline

Make today a breakthrough. The SMA Drug Pipeline is how Cure SMA evaluates the success of our spinal muscular atrophy (SMA) research program. It identifies […]

Drug Discovery

Make today a breakthrough. Drug discovery takes what we’ve learned about the causes and biology of spinal muscular atrophy (SMA) and utilizes it for basic […]

Thank You for a Wonderful 2022 Annual SMA Conference!

Posted in Conference, Front Page News

Thank you to everyone who attended the 2022 Annual SMA Conference at the Disneyland Hotel in Anaheim, California! It was an impactful weekend of opportunities […]

Cure SMA Releases Updated Drug Pipeline

Posted in Clinical Trials, Front Page News, Our Impact, Research

We’ve recently released an update to the SMA drug pipeline. This latest version includes: 20 active programs, including three approved therapies. 10 pharmaceutical partners. 12 […]

Scholar Rock Shares SMA Community Letter and Announces Design of Phase 3 SAPPHIRE Clinical Trial

Posted in Front Page News, Industry Updates, Research

Dear SMA Community, We are excited to announce the design of SAPPHIRE, a Phase 3 clinical trial to further evaluate the safety and efficacy of […]

New Data Presented at World Muscle Society 2021 Virtual Congress

Posted in Front Page News, Industry Updates, Research

This week, new data was presented at the World Muscle Society 2021 Virtual Congress. Check it out below! Scholar Rock presents two posters […]

Thank You for Another Fantastic Virtual SMA Conference!

Posted in Conference, Front Page News

Cure SMA would like to thank everyone who attended the recent 2021 Virtual SMA Conference and 2021 Virtual SMA Research & Clinical Care Meeting. It was an impactful […]

Community Statement from Genentech

Posted in Front Page News, Industry Updates

Dear SMA Community, Based on our commitment to the SMA community to provide transparent, timely updates related to our medicines, we are writing to share […]