Spinal muscular atrophy (SMA) is the leading genetic cause of death for infants. However you are impacted, we have information and resources to support your needs.
News Feed
Results from Genentech’s Evrysdi Study in Infants with Type 1 SMA Published in NEJM
Genentech, a member of the Roche Group, announced in a press release that Evrysdi™ (risdiplam) data from the dose finding Part 1 ...
Cure SMA Launches Virtual Therapy Program for Adults with SMA
Adults with spinal muscular atrophy (SMA) are invited to take advantage of Cure SMA’s latest support resource, the Adults with SMA Virtual ...
Cure SMA Coronavirus (COVID-19) Information Center
Despite the new reality of postponed events, remote working, and social distancing, Cure SMA would like you to ...
Community Spotlight
Community Spotlight: I am…Viola Dwyer
February 28 is Rare Disease Day. Throughout the month—in recognition of our Redefining Rare initiative—we have been posting stories about SMA ...
Jessica’s Story: Remembering Piper Grace
February 28 is Rare Disease Day. Throughout the month—in recognition of our Redefining Rare initiative—we will be posting stories about SMA ...
Community Spotlight: I Am…Kelsey Roberts
February 28 is Rare Disease Day. Throughout the month—in recognition of our Redefining Rare initiative — we will be posting stories ...
Cure SMA is committed to local support.
Find resources or a treatment site in your area.
Since 1984, we’ve invested $82 million in the research that has made today’s breakthroughs possible. We advance a comprehensive research program, attacking SMA from all sides.
The Cure SMA Care Center Network
Local, evidenced-based care centers, designed to develop an evidence-based standard of care to improve the lives of all those affected by SMA.