Annual SMA Research & Clinical Care Meeting

The Annual SMA Research & Clinical Care Meeting is the largest meeting of its kind in the world focused on spinal muscular atrophy (SMA) and offering insightful discussion around new research and clinical care practices.

The Annual International SMA Research & Clinical Care Meeting brings together researchers from academia, government, and biotech/pharmaceutical companies with multi-disciplinary healthcare providers who are diagnosing and caring for people with SMA. The event is held in conjunction with Cure SMA’s Annual SMA Conference.

Man giving a speech at SMA research and clinical care conference.

Goals for SMA Research & Clinical Care Meeting

Create open communication of early, unpublished scientific data, accelerating the pace of research

Foster collaborations, including cross-disciplinary knowledge sharing, integration of researchers and drug companies, and dialogue among new and leading clinicians

Facilitate collaborative discussions between new and leading clinicians to achieve improved care for SMA

Promote conversations between the SMA community and clinicians, researchers, and industry partners

2025 Annual SMA Research & Clinical Care Meeting

The 2025 Annual SMA Research & Clinical Care Meeting will be held in Anaheim, California from Wednesday, June 25 – Friday, June 27, 2025, at Disney's Grand Californian Hotel. Bringing together researchers from academia, government, and biotech/pharmaceutical companies with multi-disciplinary healthcare providers who are diagnosing and caring for people with SMA, the Annual Research & Clinical Care Meeting is the largest meeting dedicated to SMA research and care. We look forward to reuniting the community at this 29th annual meeting to learn about the latest advances in research, treatments, and care.

As always, the Annual SMA Conference and Research & Clinical Care Meeting run in parallel with each other. Through these meetings, we bring together researchers, healthcare professionals, and families to network, learn, and collaborate. If you have any questions, please reach out to [email protected].

Photo from a Research and Clinical Care conference presentation.

Abstract Submission

We welcome all abstract submissions on any topic related to SMA. Your contributions are vital to advancing our collective understanding and improving outcomes for individuals with SMA. We ask that all abstract submissions for talks be on new and unpublished data.

This year, based on your feedback, we are planning to integrate some of the clinical care and basic research topics into comprehensive sessions of the meeting. We are planning sessions that highlight the following topics:

Dual Treatment or Combination Therapy (biological evidence in support of/against to clinical observation/experience)
Scoliosis and Orthopedic Interventions
Neurocognition and brain structure/function
Rehabilitation Recommendations: (examples may include bracing, novel equipment, and school accommodations)

We are also interested in exploring other relevant topics, such as peripheral manifestations of disease, genitourinary and renal concerns, and pre-op and post-op surgical management.

Deadline to submit abstracts is Friday, March 7^th. Notification of acceptance will occur on or before April 4^th.

Click Here To Submit An Abstract

The Clinical Care Session of the 2025 Annual Cure SMA Research and Clinical Care Meeting Accreditation:

Information on CME coming in 2025.

Research & Clinical Care Meeting Schedules

Schedules will be available in 2025.

2025 Annual Research Meeting Sponsors

The research portion of the 2025 Annual SMA Research & Clinical Care Meeting is made possible by the generosity of our sponsors and supporters.

Presenting Sponsor

Diamond Sponsor

Novartis

Title Sponsor

Expo Convention Contractors

Supporting Sponsors

The Dhont Family Foundation
The Jacob Isaac Rappoport Foundation
Luke 18:1

Gold Sponsor

Frequently Asked Questions

The following are some of the most frequently asked questions about the Annual SMA Research & Clinical Care Meeting. If you have additional questions, please email [email protected].

What is the cost of registration?

Regular Registration

$1,200 for Industry

$550 for Academic Researcher/PI

$325 Student/Fellow/Trainee/Non-Physician HCP

Late Registration Prices for R/CC (effective May 10th)

$2,000 for Industry

$650 for Academic Researcher/PI

$375 Student/Fellow/Trainee/Non-Physician HCP

Onsite pricing is as follows (effective May 24th)

$2,500 for Industry

$750 for Academic Researcher/PI

$400 for Student/Fellow/Trainee/Non-Physician HCP

What is the cost to add on the Community Conference?

Community Conference Add-On: $275

If you wish to attend the Annual SMA Conference intended for individuals living with SMA and their families and caregivers, please select this add-on. Please note that joint Annual SMA Conference and Annual SMA Research & Clinical Care Meeting events such as the Meet & Greet and Family Friendly Poster Session do not require this add-on to attend.

What is the discounted room rate at the Disneyland Grand Californian?

Are refunds provided for registration if I cannot attend?

Starting in November 2024, all attendees paying for registration will be charged the processing fees related to the purchase. This applies to registration fees of all types. This fee is not refundable in any circumstances (including errors, refunds, discounts applied later, etc.).

The deadline for refund requests is May 2, 2025 (refunds will NOT include transaction fees).

Refund requests will not be considered after this date.

Any requests for transfers or swaps will not be honored.

Are attendees of the Research & Clinical Care Meeting able to utilize the children's program?

Please note, that the Children’s Program offered for Community Conference Attendees is NOT available for Research or Clinical Care attendees and their families due to the large volume of community conference attendees.

Additional family members do need to be registered for the Community Conference to be able to attend any of the Community Conference events, such as the Meet & Greet, Family Friendly Poster Session, PJ Party, and other special events! Please contact [email protected] for further information.

Will Cure SMA be offering CME/CE credit at the meeting?