Latest Advances

Cure SMA shares a variety of different research-focused updates with our spinal muscular atrophy (SMA) community. Check out the various types of announcements below and visit Latest News for updates.


Basic research grant awards

Every spring, we announce the recipients of our basic research grants. They are researchers pursuing the most promising ideas that can lead to new SMA treatments.


Drug discovery grant awards

Periodically, we announce new drug discovery funding. These grants help turn basic research ideas into specific drug candidates that can be tested in clinical trials.


Clinical trial recruitment announcements

We regularly post information about clinical trials that are currently recruiting participants. Depending on several factors, you may choose to enroll yourself or your child in a clinical trial.


Data releases

Clinical trial sponsors periodically release data from ongoing trials.


Regulatory updates

Once a clinical trial is completed, the sponsor will evaluate all the data. If the data shows the drug is safe and effective, the sponsor will file for approval with government regulators.



After the FDA and international regulators review a drug for safety and effectiveness, they will issue a ruling. If the drug is approved, doctors can then begin to prescribe it to eligible patients.

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