Latest Advances

Cure SMA shares a variety of different research-focused updates with our spinal muscular atrophy (SMA) community. Check out the various types of announcements below and visit Latest News for updates.

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Basic research grant awards

Every spring, we announce the recipients of our basic research grants. They are researchers pursuing the most promising ideas that can lead to new SMA treatments.

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Drug discovery grant awards

Periodically, we announce new drug discovery funding. These grants help turn basic research ideas into specific drug candidates that can be tested in clinical trials.

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Clinical trial recruitment announcements

We regularly post information about clinical trials that are currently recruiting participants. Depending on several factors, you may choose to enroll yourself or your child in a clinical trial.

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Data releases

Clinical trial sponsors periodically release data from ongoing trials.

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Regulatory updates

Once a clinical trial is completed, the sponsor will evaluate all the data. If the data shows the drug is safe and effective, the sponsor will file for approval with government regulators.

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Approval

After the FDA and international regulators review a drug for safety and effectiveness, they will issue a ruling. If the drug is approved, doctors can then begin to prescribe it to eligible patients.

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