Published APNCR Research

The Adult & Pediatric Neuromuscular Clinical Research Network (APNCR) develops and refines outcome measures for spinal muscular atrophy (SMA), conducts clinical trials for new treatment approaches, and conducts research to evaluate the impact of approved treatments to help support broad access. Published research from APNCR may be found below.

 

APNCR Publications

2025

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2024

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2023

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2022

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2021

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2020

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2019

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2018

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Since 2012, the Trainor family has been building an endowment at Cure SMA to support several critical strategic initiatives. In the most recent year, the Erin Trainor Memorial Fund committed support to the efforts of the APNCR network. Cure SMA thanks the Trainors and their friends and family for specifically supporting the strategic goal of bringing new and especially adult-focused treatment and care hospitals into this important network.

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