SMA Treatment Delay FAQ

We know our community has many pressing questions related to the FDA approval delay of Scholar Rock’s apitegromab. This FAQ was developed to address the most common concerns and provide the latest updates as we continue to work closely with Scholar Rock and the FDA.

Biogen's High Dose SPINRAZA (nusinersen), originally featured on this FAQ page, has been removed due to its FDA approval. Learn more about this approval here.

Scholar Rock's ISEMBYLD™ (apitegromab-mstn), originally featured on this FAQ page, has been removed due to its FDA approval. Learn more about this approval here.