Cure SMA leads the way to a world where everyone impacted by spinal muscular atrophy is empowered to lead independent, successful, and fulfilling lives.
Our powerful progress includes:
- Three approved treatments for SMA
- Newborn screening across 100% of the U.S.
- More clinical trials happening than ever before
However, our work is not over, and we need your support.
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Spinal muscular atrophy (SMA) is a progressive neurodegenerative disease that affects the motor nerve cells in the spinal cord and impacts the muscles used for activities such as breathing, eating, crawling, and walking.
Cure SMA is committed to local support.
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