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First ever SMA regulatory filings to be submitted.

Check out our news section for the latest updates on this important milestone.

Check out our events calendar to see a full
list of events happening in your area!

Check out the latest updates from the
2016 Annual SMA Conference.

Through information packets, care packages, local chapters, equipment, and resources, we support families today.

We now have 18 programs in the SMA drug
pipeline. Together, we're making real
progress toward a treatment and a cure.

September 23, 2016

Roche has officially launched two Phase 2 clinical trials testing RO7034067 (also known as RG7916). The trials will begin recruitment in...

September 19, 2016

Over the last decade, we’ve seen many advances in spinal muscular atrophy research, from new techniques in gene therapy to drugs that show...

September 16, 2016

Roche, PTC Therapeutics, and the SMA Foundation have released a community update on the development of their SMN2 splicing modifier clinical...

September 14, 2016

The SMA Researcher Meeting is the largest research meeting in the world...

September 13, 2016

Recently, Cure SMA confirmed three new board members and one new committee member. These new members will provide additional leadership in the...

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