December Webinar on SMA Treatments and Clinical Trials Now Available Online

A recording of the December 13th webinar updating the community on SMA treatments and clinical trials is now available online. A PDF of the webinar presentation is also available for download.

An update on the status of dosing for Spinraza across the United States included the following information:

  • As of October 2018, ~2,700 patients have been dosed
  • 159 sites in 44 states and DC are listed on Cure SMA’s website
  • Globally, ~6,000 patients have been dosed

Additionally, an update was given on the status of AVXS-101, now known as ZOLGENSMA. An overview of recruiting clinical trials was also presented as part of the webinar.

Thank you to everyone who tuned in and sent in their questions!

View the webinar 

Download the presentation 

Learn More

For more information about Spinraza, visit

For more information about ongoing SMA clinical trials, visit our Trials Currently Recruiting page

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