Front Page News
Meet Winnie, the 11-Year-Old Author Helping Kids Face Surgery
Winnie is an 11-year-old living with spinal muscular atrophy (SMA) who loves musicals, drawing, and playing sports with her brothers. After her recent surgery, she […]
Cure SMA Launches Their “This Gen Next 10” Campaign
Today, Cure SMA is proud to launch our year-end campaign: This Gen, Next 10. It’s a chance to look at where this community started, how […]
Adults with SMA Share Their Unmet Needs and Independence Barriers in Washington D.C.
This week, the unmet health and everyday living needs of adults with spinal muscular atrophy (SMA) took center stage in Washington, DC, in an event […]
Biogen Shares Update on the Salanersen Development Program
(opens in new tab) From newly opened Phase 3 studies enrolling infants through adults to the first participants already dosed in the U.S. and Japan, […]
Scholar Rock Receives Approval for ISEMBYLD™ for the Treatment of SMA
Scholar Rock today announced that it has received approval from the U.S. Food and Drug Administration (FDA) for ISEMBYLD™ (apitegromab-mstn) to treat spinal muscular atrophy […]
Genentech Shares Highlights from an Unforgettable Week at the Annual SMA Conference
(opens in new tab) From a lively “Evryday Café” exhibit hall experience to an advocacy reception featuring conversations on policy and access, Genentech recaps a […]
Novartis Highlights Accessible Travel Partnership in Summer Community Update
From their time at the Cure SMA Annual Conference, to their SMAshing My Limits partnership with Becoming rentABLE, opening up accessible beach houses, treehouses, and […]
Newly published research from Cure SMA: What helps young adults with SMA successfully transition to adult care?
As increased treatment options have helped more people with spinal muscular atrophy (SMA) live longer, healthier lives, more young adults are navigating the transition to […]
Thank you to everyone who attended the 2026 Annual SMA Conference
Thank You Thank you to everyone who attended the 2026 Annual SMA Conference at Disney’s Yacht & Beach Club Hotel in Orlando, Florida! It […]
Biogen Shares Conference Highlights and New High Dose SPINRAZA Resources
From the High Dose SPINRAZA symposium to a family-friendly poster session, Biogen recaps their experience at this year’s Annual SMA Conference and highlights new tools […]