Family Friendly Research Poster Session Presenters Announced

The Family Friendly Research Poster Session will be held on Saturday, June 29th from 6:30pm to 8:00pm at the 2019 Annual SMA Conference. 

The Family Friendly Research Poster Session allows for one-on-one interactions between families and researchers. Cure SMA has invited researchers, who are attending SMA Researcher Meeting, to present family friendly research posters. During the event, families are encouraged to rotate to the different posters to ask questions and learn directly from the researchers involved in each of the projects being presented.

  1. Allison Ebert, PhD from the Medical College of Wisconsin: Understanding SMN function in Different Cell Types
  2. Allison Mazzella from Cure SMA: Assessing Clinical Meaningfulness and Patient Experience in the SMA Teen and Young Adult Populations
  3. Arthur Burghes, PhD & Anton Blatnik from the Ohio State University: Suppressors of SMN Function and Modifiers of Spinal Muscular Atrophy
  4. Janice Wong, MD & Kristina Johnson from Biogen: The Spinraza Clinical Development Program
  5. Garrett Ingrando, MBA from Biogen: SPINRAZA Experience in the Real World
  6. Brunhilde Wirth, PhD from the University of Cologne, Germany: Genetic modifiers of SMA Help Some People to Remain Asymptomatic; How Can This Knowledge Help All People with SMA?
  7. Cera Hassinan from Johns Hopkins School of Medicine: Neurofilament as a biomarker for SMA
  8. Chad Heatwole, MD, MS-CI from University of Rochester Medical Center: Measurement of a Patient’s Health Status (The SMA-Health Index)
  9. Geneviève Paris & Andréanne Didillon from the University of Ottawa: SMN and friends: What we can learn from SMN Interactors
  10. Jen Szegda & Erin Treece, MS from Scholar Rock: SMA Muscle-Directed Therapy Advancing in Clinical Development.
  11. Hannah Staunton & Samuel Ewing, EngD from F. Hoffmann-La Roche: New measures of function and independence in Spinal Muscular Atrophy
  12. Jamie Shish from Cure SMA: Cure SMA Newborn Screening Survey and Database
  13. Reid Garner, Christiano R Alves, PhD, Kathryn J Swoboda, MD from Massachusetts General Hospital & Harvard Medical School: Circulating biomarkers for Spinal Muscular Atrophy
  14. Senam Beckley-Kartey, Marco Castillo, MD & Fani Petridis from F. Hoffmann-La Roche: Roche and Genentech Spinal Muscular Atrophy Clinical Development Program
  15. Kevin Kaifer, PhD from the University of Missouri: Astrocytes Contribute to Motor Neuron Degeneration in Spinal Muscular Atrophy
  16. Zaida Alipio-Gloria, Arnab K. Chatterjee, Jingxin Wang, Andrew To, Kristen Johnson from Calibr, a Division of Scripps Research: Innovative Screening Approaches to Identify the Next Generation of SMN-Inducing Compounds 
  17. Frank Bennet, PhD & Kristina Bowyer from Ionis Pharmaceuticals: Antisense Oligonucleotide Strategies for SMA
  18. Krysta Engel, PhD from the University of Colorado: Transcriptome-Wide Interrogation of SMN-mediated RNA Localization Mechanisms in Neurons
  19. Laxman Gangwani, PhD from Texas Tech University: Overview and Comparison of SMN-Dependent and SMN-Independent Methods for the Treatment of Spinal Muscular Atrophy 
  20. Lisa Belter from Cure SMA: Cure SMA Membership: Findings from the 2019 Membership Survey
  21. Samantha Edell, Darren T. Hwee, PhD, Stacy Rudnicki, MD, Bettina Cockroft, MD, MBA, Andrew Wolff, MD & Lucie Vu, PharD from Cytokinetics: Results from Two Pre-clinical Studies: Reldesemtiv in Combination with Nusinersen and in Combination with SMN-C1 Shows Improved Muscle Function in Mouse Model of Spinal Muscular Atrophy
  22. Mary Schroth, MD, Jamie Shish, Teresa Stewart & Abigail Paras from Cure SMA: Cure SMA Clinical Care Center Network and SMA Clinical Data Registry
  23. Doug Sproule, MD from AveXis: Provide an overview of ZOLGENSMA indication, efficacy, safety and dosing for Caregivers
  24. Kathy L. Poulin, Joshua Del Papa, Hugh J. McMillan, MD, Jodi Warman Chardon, MD, Rashmi Kothary,PhD & Robin J. Parks, PhD from the Ottawa Hospital Research Institute: Biomarkers for Spinal Muscular Atrophy
  25. Samuel R. Rosenfeld, MD from Children’s Hospital of Orange County: 20 Year Experience with Segmental Sublaminar Instrumentation for Guided Growth in Early Onset Scoliosis
  26. Bakri Elsheikh, MD & Sarah Heintzman, RN from the Ohio State University: The Spinraza Treatment Initiative at The Ohio State University
  27. Saravanan Arumugam, Michael Kahl, Zhaofa Xu & Yongchao Ma, PhD from Northwestern Unviersity: Targeting Mitochondria, the Powerhouse in Motor Neurons, for Treating SMA
  28. Fernanda Boulos, PhD and Svetlana Jevtic, DVM, Msc from Novartis: Branaplam (LMI070) clinical program summary
  29. Sibylle Jablonka, PhD & Utz Fischer, PhD from the University of Wuerzburg, Germany: Calcium Channels in SMA: What about the SMN complex?
  30. Erin Kelly from Cure SMA: The SMA Patient and Family Voice: Impacting our Community and Stakeholders Through Advocacy, Clinical Care, Research, and Industry Partnerships
  31. Josh Noone, PhD, Sarah Whitmire, MS, Daniel Buchenberger, MS, Rosalina Mills, Christine Pozniak, PhD & Er Chen, MPP from F. Hoffmann-La Roche: Impact of SMA on Caregivers’ Daily Activities and Health-Related Quality of Life

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