Check Out Cure SMA’s State of SMA Report
Cure SMA is pleased to announce the launch of its first annual State of SMA report. The purpose of this report is to share highlights from Cure SMA’s three databases: the membership database ...
Traveling with SMA
As the summer season nears, many families will make plans to travel across the country to exciting destinations or to spend time with those they love. This is no different for those affected ...
Cure SMA Awards $150,000 Grant to Charlotte Sumner, MD, Johns Hopkins University
Cure SMA has awarded a $150,000 research grant to Charlotte Sumner, MD, at Johns Hopkins University, for her project, "Testing the potential of SMN-AS1 as a therapeutic target in SMA.”Dr. Sumner and her ...
The Discovery of SMA
In 2016, the spinal muscular atrophy community celebrated the approval of the first-ever treatment that targets the underlying genetic cause of SMA. This was a milestone more than 100 years in the making, ...