Latest News
#ShowYourRare and Raise SMA Awareness on World Rare Disease Day
Rare Disease Day is today, February 28! And we’re calling on our entire spinal muscular atrophy community to get involved. Rare Disease Day is important to us because it is […]
Read More ›Last Week’s Webinar on Treatment Access and Clinical Trials Now Available
A recording of last week’s webinar updating the community on treatment access and clinical trials is now available online. A PDF of the webinar presentation is also available for download. […]
Read More ›Cure SMA Receives Generous Gift from the Weisman Family Foundations
The Weisman Family Foundations recently awarded $65,800 to Cure SMA, in order to further new scientific research, and to help provide access to treatments, clinical trials and care. Each year, […]
Read More ›Phase 2 Clinical Trial Results for CK-2127107 Expected in Second Quarter of 2018
Cytokinetics is currently conducting a Phase 2 clinical trial of CK-2127107 – now referred to by the generic name, reldesemtiv – which is designed to assess the investigational agent’s effect […]
Read More ›Cure SMA Receives Generous Gift
Cure SMA is extremely pleased to announce a generous $620,000 gift has been made to the organization. The donation was made anonymously in honor of William N. Kanehann. Billy had […]
Read More ›Biogen Releases Statement on CHERISH Data and Plans for New Clinical Research
Biogen has provided the following community statement on the final results from CHERISH, a Phase 3 study of SPINRAZA. Dear Members of the SMA community, This past December marked one […]
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