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Biogen Announces Advancement of Investigational SMA Drug Salanersen to Registrational Trials Based on Positive Phase 1 Results

June 25, 2025
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“To see a child dosed with gene therapy at age one and still unable to sit at age five then gain that ability within three […]

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Cure SMA Awards $149,202 Grant to Rico Schieweck, PhD, at the Luxembourg Center for Systems Biomedicine (LCSB)

June 24, 2025
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Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA […]

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Cure SMA Awards $50,000 Grant to Tianyuan Shi, PhD, at the University of Hong Kong

June 21, 2025
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Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA […]

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Cure SMA Awards $150,000 Grant to Charlotte Sumner, MD, at Johns Hopkins University School of Medicine

June 20, 2025
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Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA […]

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Cure SMA Celebrates Dr. Mary Schroth as she Retires as Chief Medical Officer

June 10, 2025
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We are honored to celebrate the incredible contributions of Dr. Mary Schroth, who is retiring after seven years as our Chief Medical Officer and after […]

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New Advocacy Resource: Explore the Cure SMA State and Local Toolkit!

June 9, 2025
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Make an Impact in Your State and Community Cure SMA is proud to announce the launch of our brand-new State and Local Advocacy Toolkit, now […]

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Understanding Gene Therapy: A Cure SMA Video

May 19, 2025
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A drug’s mechanism of action, or MOA, refers to how a drug or other substance produces an effect in the body. Understanding a drug’s mechanism […]

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Double Your Power, Double Our Progress: Help Cure SMA Unlock $150,000 for SMA Research!

May 19, 2025
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During our Nunemaker Family Research Community Challenge, all donations will be matched up to $150,000! Cure SMA is proud to announce the launch of our […]

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Last Chance to Participate in the Annual Cure SMA Community Update Survey

May 16, 2025
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Since 2017, the Cure SMA Community Update Survey has collected data and information on the SMA community’s experiences and unmet needs. Every single individual with […]

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Novartis Gene Therapies Releases Spring SMA Community Update Letter

May 5, 2025
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Novartis Gene Therapies recently released an update on their continued collaboration with the SMA community through events, advisory boards, clinical insights, and ongoing efforts to […]

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