Front Page News
Biogen Announces Advancement of Investigational SMA Drug Salanersen to Registrational Trials Based on Positive Phase 1 Results
“To see a child dosed with gene therapy at age one and still unable to sit at age five then gain that ability within three […]
Read More ›Cure SMA Awards $149,202 Grant to Rico Schieweck, PhD, at the Luxembourg Center for Systems Biomedicine (LCSB)
Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA […]
Read More ›Cure SMA Awards $50,000 Grant to Tianyuan Shi, PhD, at the University of Hong Kong
Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA […]
Read More ›Cure SMA Awards $150,000 Grant to Charlotte Sumner, MD, at Johns Hopkins University School of Medicine
Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA […]
Read More ›Cure SMA Celebrates Dr. Mary Schroth as she Retires as Chief Medical Officer
We are honored to celebrate the incredible contributions of Dr. Mary Schroth, who is retiring after seven years as our Chief Medical Officer and after […]
Read More ›New Advocacy Resource: Explore the Cure SMA State and Local Toolkit!
Make an Impact in Your State and Community Cure SMA is proud to announce the launch of our brand-new State and Local Advocacy Toolkit, now […]
Read More ›Understanding Gene Therapy: A Cure SMA Video
A drug’s mechanism of action, or MOA, refers to how a drug or other substance produces an effect in the body. Understanding a drug’s mechanism […]
Read More ›Double Your Power, Double Our Progress: Help Cure SMA Unlock $150,000 for SMA Research!
During our Nunemaker Family Research Community Challenge, all donations will be matched up to $150,000! Cure SMA is proud to announce the launch of our […]
Read More ›Last Chance to Participate in the Annual Cure SMA Community Update Survey
Since 2017, the Cure SMA Community Update Survey has collected data and information on the SMA community’s experiences and unmet needs. Every single individual with […]
Read More ›Novartis Gene Therapies Releases Spring SMA Community Update Letter
Novartis Gene Therapies recently released an update on their continued collaboration with the SMA community through events, advisory boards, clinical insights, and ongoing efforts to […]
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