Front Page News
FDA Issues Statement on Data Accuracy Issues with Recently Approved Gene Therapy
Today, the FDA issued the below statement identifying data accuracy issues with AveXis’ SMA therapy, Zolgensma. Cure SMA is investigating this issue and will report when we have […]
Read More ›Biogen Issues Community Statement on Spinraza
Biogen has provided the following community statement on Spinraza. Dear members of the SMA community, Following a busy spring of data presentations at medical congresses […]
Read More ›SMA Awareness Month 2019 Has Begun!
SMA Awareness Month occurs in August! The SMA community officially recognizes August as Spinal Muscular Atrophy Awareness Month and Cure SMA has been coordinating activities […]
Read More ›Biogen Announces New NURTURE Data at the 2019 Annual SMA Conference
Biogen today announced new results from the NURTURE study, adding data to the longest study of spinal muscular atrophy (SMA) in pre-symptomatic infants (n=25). These […]
Read More ›Updated SMA Drug Pipeline Now Available
We’ve recently released an update to the SMA drug pipeline. This latest version includes: 23 active programs, including two approved therapies. 15 pharmaceutical partners. 6 […]
Read More ›Cytokinetics Releases New Data from Reldesemtiv Clinical Study at the 2019 Annual SMA Conference
Cytokinetics, Incorporated, today announced that data from two preclinical studies of reldesemtiv were presented at the 2019 Annual Cure SMA Conference in Anaheim, CA, showing […]
Read More ›The 2019 Annual SMA Conference is Here!
The 2019 Annual SMA Conference, now in its 31st year, is set to kick off on June 28 and continue into a weekend full of […]
Read More ›Cure SMA Receives $150,000 Grant From the Oscar G and Elsa S Mayer Family Foundation
Cure SMA is pleased to announce receipt of $150,000 grant over three years, awarded by the Oscar G. and Elsa S. Mayer Family Foundation to […]
Read More ›Community Spotlight: Laura Watson
Laura Watson is team captain of Laura’s Dream Team and fundraising committee co-chair of the North New Jersey Cure SMA Chapter. On Saturday, June 22, […]
Read More ›The 2019 Annual SMA Conference Booklet is Now Posted Online
The 2019 Annual SMA Conference booklet is now available for download. The booklet includes information on workshops, special events and details of the Annual SMA […]
Read More ›