Front Page News
Community Spotlight: Rebecca Smith and Micah Biello
When Micah Biello was diagnosed with spinal muscular atrophy type 1, no one in his family knew about the disease. Now four years later, Micah’s […]
Read More ›Genentech, Roche and PTC Therapeutics Provide Update on Regulatory Filing for Risdiplam
On January 7th, PTC Therapeutics, Inc. provided a corporate update, which will be detailed as part of the company’s presentation at the 37th Annual J.P. […]
Read More ›Teen and Young Adult Survey Extended Through January 21st
Are you or a family member between the ages of 12 and 25? Do you want to share your opinion on living with SMA and […]
Read More ›Community Spotlight: The Jankowski Family
It has been a little over two years since doctors told Chris and Kelly Jankowski that their first-born son, William, had spinal muscular atrophy (SMA) […]
Read More ›Cure SMA Announces Expanded Phase 3 of SMA Industry Collaboration
Cure SMA is pleased to announce the launch of an expanded Phase 3 of our SMA Industry Collaboration. The SMA Industry Collaboration is a multi-faceted […]
Read More ›Hope on the Hill Congressional Dinner Raises $200,000
The 8th Annual “Hope on the Hill” Congressional Dinner was held on Tuesday, November 27, 2018 at The Willard Hotel in Washington, DC. More than […]
Read More ›December Webinar on SMA Treatments and Clinical Trials Now Available Online
A recording of the December 13th webinar updating the community on SMA treatments and clinical trials is now available online. A PDF of the webinar […]
Read More ›2018 Research Year-in-Review
Over our past fiscal year—from July 1, 2017, to June 30, 2018—Cure SMA has funded over $5 million in new research funding. This funding will be […]
Read More ›Cure SMA Funding Leads to 16 New Research Publications in 2018
An important goal of our research funding strategy is to share scientific findings with the broader scientific community. Scientists who receive Cure SMA funding often […]
Read More ›Community Spotlight: The Berkovits Family
When Milo Berkovits was seven months old, his daycare teacher noticed he was not reaching his milestones. What followed from there on were visits to […]
Read More ›