Latest News
2015 Family Friendly Poster Session Presenters Announced
The Family Friendly Research Poster Session is one of the most anticipated events of our Annual SMA Conference. Each year, Cure SMA invites researchers from the SMA Researcher Meeting, which […]
Read More ›Update on Clinical Development of RG7800
F. Hoffman-La Roche, PTC and the SMA Foundation recently provided an update on the clinical development of RG7800, an investigational SMN2 splicing modifier that is being studied as a potential […]
Read More ›Cure SMA Funds $1.85 Million in New Research Grants in 2014-2015
Over the past few months, Cure SMA has announced a total of $1.85 million in new research funding. Our model is designed to fund both a breadth and a depth […]
Read More ›Cure SMA Announces Additional $445,000 for Nationwide Children’s Hospital Gene Therapy Program led by Brian Kaspar, PhD
Cure SMA, the leading organization dedicated to the treatment and cure of spinal muscular atrophy (SMA), recently provided an additional $445,000 grant toward a gene therapy for SMA at Nationwide […]
Read More ›New 21st Century Cures Discussion Draft Released
The US House of Representatives Energy and Commerce Committee has released a new 21st Century Cures discussion draft. This is a revised and expanded version of the first draft that […]
Read More ›Registration for the 2015 Annual SMA Conference Closes in Two Weeks
The deadline to register for our Annual SMA Conference is just two weeks away. Registration will close on Friday, May 9. Over 1,000 people have already registered—don’t miss your chance […]
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