Latest News
Biogen Announces Advancement of Investigational SMA Drug Salanersen to Registrational Trials Based on Positive Phase 1 Results
“To see a child dosed with gene therapy at age one and still unable to sit at age five then gain that ability within three months of starting salanersen is […]
Read More ›Cure SMA Awards $149,202 Grant to Rico Schieweck, PhD, at the Luxembourg Center for Systems Biomedicine (LCSB)
Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA biology. Our Scientific Advisory Board […]
Read More ›Cure SMA Awards $50,000 Grant to Tianyuan Shi, PhD, at the University of Hong Kong
Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA biology. Our Scientific Advisory Board […]
Read More ›Cure SMA Awards $150,000 Grant to Charlotte Sumner, MD, at Johns Hopkins University School of Medicine
Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA biology. Our Scientific Advisory Board […]
Read More ›Cure SMA Celebrates Dr. Mary Schroth as she Retires as Chief Medical Officer
We are honored to celebrate the incredible contributions of Dr. Mary Schroth, who is retiring after seven years as our Chief Medical Officer and after many decades of service and […]
Read More ›New Advocacy Resource: Explore the Cure SMA State and Local Toolkit!
Make an Impact in Your State and Community Cure SMA is proud to announce the launch of our brand-new State and Local Advocacy Toolkit, now available on the Advocacy webpage! […]
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