Latest News
Grant Announcement: Cure SMA Awards a $170,000 Grant to Lyndsay Murray, Ph.D., University of Edinburgh
This article is part of a series of Cure SMA grant announcements that will be shared throughout the next couple of months. Cure SMA has awarded a $170,000 research grant […]
Read More ›Cure SMA Working Group Revises Recommendations for the Treatment of Infants Diagnosed with SMA via Newborn Screening Who Have 4 Copies of SMN2
To help clinicians and the families they serve in the decision of when to administer therapy to infants identified with SMA via newborn screening, Cure SMA convened a working group […]
Read More ›Cure SMA Launches “Spotlight on SMA” Partnership with Neurology Reviews
Cure SMA is pleased to announce the release of “Spotlight on SMA: The Urgent Need for Early Diagnosis in Spinal Muscular Atrophy,” a supplement developed in collaboration with Neurology Reviews. […]
Read More ›Celebrate Rare Disease Day 2020 with Cure SMA
This year, Rare Disease Day occurs on February 29—the rarest day of all! Spinal muscular atrophy (SMA) affects 12,000 people in the U.S. Yet, the SMA community is part of […]
Read More ›Lights…Camera…Action! Search Is On for Child with SMA to Appear in NBC Television Pilot
Cure SMA is excited to support casting directors from NBC as they search for boys and girls from the SMA community who are interested in playing a character with spinal […]
Read More ›Genentech’s Risdiplam Showed Significant Improvement in Motor Function in People Aged 2-25 Years with Type 2 or Type 3 SMA
Genentech, a member of the Roche Group, today presented 1-year data from the pivotal Part 2 of the SUNFISH study, evaluating risdiplam in people aged 2-25 years with Type 2 […]
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