Research
Summer 2017 Update to SMA Drug Pipeline is Released
We’ve recently released an update to the SMA drug pipeline. This latest version includes: 19 active programs, including one approved therapy. 14 pharmaceutical partners. 5 […]
Read More ›Cure SMA Funded Standard of Care Paper Published in Neuromuscular Disorders Journal
The journal Neuromuscular Disorders has published a paper reporting on the findings of an international workgroup convened to update the Standard of Care (SOC) for […]
Read More ›AveXis Announces Alignment with the FDA on Company’s GMP Commercial Manufacturing Process for AVXS-101
AveXis today announced alignment with the U.S. Food and Drug Administration (FDA) on the company’s Good Manufacturing Practice (GMP) commercial manufacturing process for AVXS-101 following […]
Read More ›Cure SMA Awards $140,000 Grant to Oliver Gruss, PhD, Rheinische Friedrich-Wilhelms-Universitat Bonn and Utz Fischer, PhD, Julius-Maximilians-Universitat Wurzburg, Germany
Cure SMA has awarded a $140,000 research grant to Drs. Oliver Gruss and Utz Fischer at Rheinische Friedrich-Wilhelms-Universitat Bonn and Julius-Maximilians-Universitat Wurzburg in Germany to […]
Read More ›Cure SMA Awards $140,000 Grant to Alberto Kornblihtt, PhD, Universidad de Buenos Aires, Argentina
Cure SMA and FAME (Families of SMA, Argentina) have awarded a $140,000 research grant to Alberto Kornblihtt, PhD, at the Universidad de Buenos Aires, Argentina, […]
Read More ›Cure SMA Awards $75,000 Grant to Yong-Chao Ma, PhD, Ann & Robert H. Lurie Children’s Hospital of Chicago
Cure SMA has awarded a $75,000 research grant to Yong-Chao Ma, PhD, Ann & Robert H. Lurie Children’s Hospital of Chicago, for his project, “Regulation […]
Read More ›Cure SMA Awards $75,000 Grant to Stephen J. Kolb, PhD, Ohio State University
Cure SMA has awarded a $75,000 research grant Stephen J. Kolb at Ohio State University, for his project, “Arrested Development or Neurodegeneration? An approach to […]
Read More ›Cure SMA Awards $75,000 Grant to Chris Lorson, PhD, University of Missouri
Cure SMA has awarded a $75,000 research grant to Chris Lorson, PhD, at the University of Missouri, for his project, “Examining the role of astrocytes […]
Read More ›Cure SMA Announces Increase in Basic Research Funding, Now Exceeding $1 Million in Grants
We are excited to announce that two additional grants have been added to this round of basic research funding, which brings the total to $1.03 […]
Read More ›Cure SMA Awards $140,000 Grant to Christine DiDonato, PhD, Ann & Robert H. Lurie Children’s Hospital of Chicago
Cure SMA has awarded a $140,000 research grant to Christine DiDonato, PhD, Ann & Robert H. Lurie Children’s Hospital of Chicago, for her project, “Skeletal […]
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