Research
Cure SMA Announces New $50,000 Clinical Care Research Grant to Nilesh Mehta at Boston Children’s Hospital
We’re excited to announce that we have awarded $50,000 clinical care grant to Dr. Nilesh Mehta, for his project focusing on nutrition in SMA. Some […]
Results Published on First Large Animal Model of SMA
Dr. Arthur Burghes, a Cure SMA Scientific Advisory Board Member from Ohio State University, has published a paper on the first-ever large animal model of […]
Cure SMA Funding Leads to 16 New Research Publications in 2014
An important goal of our research funding strategy is to share scientific findings with the broader scientific community. Scientists who receive Cure SMA funding often […]
Cure SMA Funds 26 Research Projects in 2014
Our strategic research approach includes four areas—basic research, drug discovery, clinical trials, and clinical care—working together toward our vision of a world without SMA. Cure […]
Isis Expands Phase 3 Clinical Trials
Isis recently announced that they have tested the first patient in CHERISH, a multi-center Phase 3 clinical study evaluating the efficacy and safety of the […]
SMA Drug Pipeline Continues to Grow
This is an exciting time for the entire SMA community, as we celebrate another year of increasing momentum toward our goal of a treatment and […]
Cure SMA Researchers Present at Society for Neuroscience Meeting
The Society for Neuroscience (SfN) Meeting is the premiere neurobiology meeting, with over 30,000 scientists in attendance each year. This year’s meeting was held November […]
PTC Therapeutics Announces New Phase 1a/2b Clinical Trial
PTC Therapeutics, Inc. announced today that its joint development program in Spinal Muscular Atrophy (SMA) with Roche and the SMA Foundation (SMAF) has started a […]
Isis Announces Second Phase III Clinical Trial
Isis recently announced the start of CHERISH, a multi-center Phase III clinical study evaluating the efficacy and safety of the investigational compound, ISIS-SMNRx, in non-ambulatory […]
Cure SMA Scientific Advisory Board Meets in Washington D.C.
Today and tomorrow, Cure SMA’s Scientific Advisory Board (SAB) will be meeting in Washington D.C. Our Scientific Advisory Board is a recognized group of experts […]