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HHS Secretary, Alex Azar, Recommends Nationwide Newborn Screening for SMA

July 4, 2018
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Health and Human Services Secretary Alex Azar today approved the recommendation that newborn screening for spinal muscular atrophy be implemented nationwide. This recommendation was issued […]

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SMA Newborn Screening Moves Forward in New Jersey

June 28, 2018
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Earlier this month, the New Jersey State Senate Committee on Health, Human Services, and Senior Citizens unanimously approved S. 974. Introduced by Senator Troy Singleton, […]

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Thank You For a Wonderful 2018 Annual SMA Conference!

June 25, 2018
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Thank you to everyone who attended the 2018 Annual SMA Conference at the Hilton Anatole Hotel in Dallas, Texas! It was an impactful weekend of […]

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Summer 2018 Issue of Compass Now Available

June 25, 2018
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The summer 2018 issue of Compass is now available online. As part of our most recent round of funding, we’ve announced ten grants totaling $1,325,000 […]

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PTC Therapeutics Announces Risdiplam (RG7916) is Well Tolerated at All Dose Levels With No Drug-Related Safety Findings

June 19, 2018
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On Saturday, PTC Therapeutics, Inc. announced the presentation of updated interim clinical data from Part 1 of the FIREFISH study investigating risdiplam (RG7916) in babies […]

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Cytokinetics Presents Data from the Phase 2 Clinical Trial of Reldesemtiv (CK-2127107) in Patients with SMA at the 2018 Annual SMA Conference

June 16, 2018
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Today, Cytokinetics announced data from the Phase 2 clinical study of reldesemtiv in patients with SMA, presented in an oral presentation by John W. Day, […]

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Biogen to Present New Data at the 2018 Annual SMA Conference

June 14, 2018
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Yesterday, Biogen announced it will present data from its SPINRAZA clinical development program –the largest of its kind, with more than six years of data–for […]

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The 2018 Annual SMA Conference is Here!

June 12, 2018
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The 2018 Annual SMA Conference, now in its 30th year, is set to kick off on June 14 and continue into a weekend full of […]

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Thank You to Our 2018 Annual SMA Conference Exhibitors!

June 11, 2018
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Thank you to the following exhibitors who are generously supporting the 2018 Annual SMA Conference. This incredible and unique event would not be possible without […]

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Traveling with SMA

June 7, 2018
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As the summer season nears, many families will make plans to travel across the country to exciting destinations or to spend time with those they […]

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