Front Page News
Spring 2016 Issue of Compass Now Available
The Spring 2016 issue of Compass is now available online. As part of our most recent round of funding, we’ve announced eight grants totaling $890,000 […]
Cure SMA Awards $300,000 Drug Discovery Grant to Charlotte Sumner, in Collaboration with Imago Pharmaceuticals
Cure SMA has awarded a $300,000 drug discovery grant to Charlotte Sumner, MD, at Johns Hopkins University, in collaboration with Imago Pharmaceuticals. The award is […]
Announcing an Evening of Fun at Disneyland Park
Just added to this year’s conference schedule: Saturday Night at Disneyland Park! We’re very excited to announce that conference attendees will get to take part […]
Cure SMA Releases Full Schedule for the 2016 Annual SMA Conference
Cure SMA has released the full schedule for the 2016 Annual SMA Conference, which will be held in Anaheim, CA at Disneyland, June 16-19. The […]
Cure SMA Awards $70,000 Grant to Christine DiDonato, Lurie Children’s Hospital of Chicago
Cure SMA has awarded a $70,000 research grant to Dr. Christine DiDonato at Lurie Children’s Hospital of Chicago for her project, “Assessing mediators of muscle […]
AveXis Reports Data from Ongoing Phase 1 Trial of AVXS-101 in Spinal Muscular Atrophy Type 1
Today, AveXis, Inc. presented an interim analysis of data as of April 1, 2016 from the ongoing Phase 1 trial of AVXS-101 for the treatment […]
Cure SMA Announces 2016 Family Friendly Poster Session Presenters
The Family Friendly Research Poster Session is one of the most anticipated events of our Annual SMA Conference. Each year, Cure SMA invites researchers from […]
Cure SMA Welcomes New Board and Committee Members
Recently, Cure SMA confirmed three new board members and several new committee members. These new members will provide additional leadership in the areas of advocacy, […]
Ionis Releases Data Update from Phase 2 Study in Infants with SMA
Ionis Pharmaceuticals provided an update on its ongoing open-label Phase 2 clinical study of nusinersen in infants with spinal muscular atrophy (SMA) at the American […]
Cure SMA and the SMA Community Featured by Astellas Pharmaceuticals
Cure SMA is featured by Astellas Pharmaceuticals as part of their new Changing Tomorrow Together website. Cure SMA Research Director Jill Jarecki contributed a spotlight […]