Front Page News
Cure SMA Testifies Before FDA at PDUFA Meeting
The Prescription Drug User Fee Act (PDUFA), the law that allows the FDA to collect fees from drug manufacturers to fund the new drug approval […]
Cure SMA Receives Generous Donation from Fighting for Kaiden Foundation
Cure SMA would like to thank the Fighting for Kaiden Foundation for their generous donations to Cure SMA programs. That generosity is providing both support […]
Biogen and Ionis Provide Update on Nusinersen (IONIS-SMNRx)
Biogen and Ionis Pharmaceuticals recently provided an update on the clinical development of nusinersen (IONIS-SMNRx), which is currently being tested in Phase 3 clinical trials: […]
Abstract Submission Opens for 2016 SMA Researcher Meeting
Abstract submission is now open for the 2016 SMA Researcher Meeting, which will be held June 16-18 as part of the Annual SMA Conference in […]
Roche Announces New Clinical Trial of RG7916
Roche, along with partners PTC Therapeutics and the SMA Foundation, recently provided the following update on the development of RG7800 and on a new clinical […]
AveXis Announces the Completion of Enrollment for Phase 1 Gene Therapy Trial
AveXis has announced that they have completed enrollment in a Phase 1 study testing systemic delivery of gene therapy for SMA. The trial has enrolled […]
Cytokinetics Opens Enrollment for Phase 2 Trial
Cytokinetics has opened enrollment for a Phase 2 study testing CK-2127107 in teens and adults with SMA type II, III or IV. We are excited […]
Cure SMA Funding Leads to 18 New Research Publications in 2015
An important goal of our research funding strategy is to share scientific findings with the broader scientific community. To help accomplish this goal, scientists who […]
Cure SMA Funds 28 Research Projects in 2015, as Drug Pipeline Grows to 18 Programs
Our approach to research is focused on continually expanding the pipeline of potential drugs and therapies for SMA, cultivating new approaches and advancing promising ideas. […]
Cure SMA Reaches Thousands of Families in 2015
Each year, Cure SMA provides thousands of families with vital support and resources to help them live active, engaged and hopeful lives. Our programs provide […]