Latest News
The 2026 Annual SMA Research & Clinical Care Meeting Summaries Are Here!
In June, SMA researchers and clinicians from around the world gathered in Orlando for the 30th Annual SMA Research & Clinical Care Meeting – to share early findings, compare notes […]
Scholar Rock Receives Approval for ISEMBYLD™ for the Treatment of SMA
(opens in new tab) Scholar Rock today announced that it has received approval from the U.S. Food and Drug Administration (FDA) for ISEMBYLD™ (apitegromab-mstn) to treat spinal muscular atrophy (SMA) […]
Genentech Shares Highlights from an Unforgettable Week at the Annual SMA Conference
(opens in new tab) From a lively “Evryday Café” exhibit hall experience to an advocacy reception featuring conversations on policy and access, Genentech recaps a full week connecting with the […]
Novartis Highlights Accessible Travel Partnership in Summer Community Update
From their time at the Cure SMA Annual Conference, to their SMAshing My Limits partnership with Becoming rentABLE, opening up accessible beach houses, treehouses, and yurts for family travel, to […]
Newly published research from Cure SMA: What helps young adults with SMA successfully transition to adult care?
As increased treatment options have helped more people with spinal muscular atrophy (SMA) live longer, healthier lives, more young adults are navigating the transition to adult care. This means moving […]
Thank you to everyone who attended the 2026 Annual SMA Conference
Thank You Thank you to everyone who attended the 2026 Annual SMA Conference at Disney’s Yacht & Beach Club Hotel in Orlando, Florida! It was an impactful weekend of […]