Latest News
Fall 2018 Issue of Directions Now Available
The Fall 2018 issue of Directions is now available online. Please visit our Support & Care Publications page to download this issue or past issues of Directions. Our biannual newsletter […]
Congratulations to the Winners of Cure SMA’s Video Contest!
Cure SMA recently hosted a video contest to raise SMA awareness and provide the opportunity for teens and young adults (aged 12 to 21) to share their experiences. The purpose […]
Community Spotlight: Rebecca Smith and Micah Biello
When Micah Biello was diagnosed with spinal muscular atrophy type 1, no one in his family knew about the disease. Now four years later, Micah’s parents, grandparents, and other family […]
Genentech, Roche and PTC Therapeutics Provide Update on Regulatory Filing for Risdiplam
On January 7th, PTC Therapeutics, Inc. provided a corporate update, which will be detailed as part of the company’s presentation at the 37th Annual J.P. Morgan Healthcare Conference. As part […]
Teen and Young Adult Survey Extended Through January 21st
Are you or a family member between the ages of 12 and 25? Do you want to share your opinion on living with SMA and what is important to you […]
Community Spotlight: The Jankowski Family
It has been a little over two years since doctors told Chris and Kelly Jankowski that their first-born son, William, had spinal muscular atrophy (SMA) type I. In the immediate […]