Our Impact
Summer 2018 Issue of Compass Now Available
The summer 2018 issue of Compass is now available online. As part of our most recent round of funding, we’ve announced ten grants totaling $1,325,000 […]
Ohio Moves One Step Closer to SMA Newborn Screening
The Ohio Newborn Screening Advisory Committee recommended that SMA be added to their state’s newborn screening panel. The recommendation now goes to the Ohio Department […]
Cure SMA Awards $150,000 Grant to Kathryn Swoboda, MD, Massachusetts General Hospital
Cure SMA has awarded a $150,000 research grant to Kathryn Swoboda, MD, at the Massachusetts General Hospital, for her project, “Clinical and pathologic correlations in […]
Spring 2018 Issue of Directions Now Available
The Spring 2018 issue of Directions is now available online. Check out our Support & Care publications page to download past issues of Directions and […]
Indiana Becomes Fourth State to Adopt Newborn Screening for Spinal Muscular Atrophy
On Friday, Governor Eric Holcomb held a signing ceremony for Indiana House Bill 1017, adopting newborn screening for spinal muscular atrophy (SMA) and severe combined […]
SMA Advocates Meet With House and Senate Offices
On Thursday, April 26, Cure SMA traveled with more than 70 spinal muscular atrophy advocates to Washington DC to meet with congressional offices. The advocates […]
Cure SMA Awards $150,000 Grant to Chad Heatwole, MD, University of Rochester
Cure SMA has awarded a $150,000 research grant to Chad Heatwole, MD, at the University of Rochester, for his project, ” Development of a Clinically […]
The Discovery of Spinraza
SMA is caused by a mutation in the survival motor neuron gene 1 (SMN1). In a healthy person, this gene produces a protein—called survival motor […]
There is Still Time to Complete Cure SMA’s 2018 Community Survey
Dear Members of the SMA Community, For the past several years, we’ve been working to collect data and information on our community’s experiences, goals, hopes, […]
Cure SMA Awards $150,000 Grant to Bakri Elsheikh, MD, Ohio State University Wexner Medical Center
Cure SMA has awarded a $150,000 research grant to Bakri Elsheikh, MD, at the Ohio State University Wexner Medical Center, for his project, “Determine the […]