Research

SMA Researchers and Clinicians from Around the World Gather at the 29th Annual SMA Research & Clinical Care Meeting

August 21, 2025
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At the end of June, SMA researchers and clinicians from around the world gathered in Anaheim, California, for the 29th Annual SMA Research & Clinical […]

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Cure SMA Awards $140,000 Grant to Mandana Arbab, PhD, at Boston Children’s Hospital

July 3, 2025
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Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA […]

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Cure SMA Awards $100,000 Grant to Yongchao Ma, PhD, at Ann & Robert H. Lurie Children’s Hospital of Chicago

July 1, 2025
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Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA […]

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Cure SMA Awards $150,000 Grant to Umrao Monani, PhD, at Columbia University Irving Medical Center

June 26, 2025
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Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA […]

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Cure SMA Awards $149,202 Grant to Rico Schieweck, PhD, at the Luxembourg Center for Systems Biomedicine (LCSB)

June 24, 2025
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Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA […]

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Cure SMA Awards $50,000 Grant to Tianyuan Shi, PhD, at the University of Hong Kong

June 21, 2025
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Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA […]

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Cure SMA Awards $150,000 Grant to Charlotte Sumner, MD, at Johns Hopkins University School of Medicine

June 20, 2025
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Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in SMA […]

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Check Out Cure SMA’s 2024 Annual State of SMA Report

March 31, 2025
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Check Out Cure SMA’s 2024 Annual State of SMA Report Cure SMA is pleased to announce the launch of our next State of SMA report, […]

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SMA Community Risk Tolerance Update: Comparison of 2022 and 2017 SMA Risk/Benefit Survey Data

March 6, 2025
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One of Cure SMA’s top priorities is to relay the SMA community’s treatment experiences and preferences to the United States Food and Drug Administration (FDA). […]

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Novartis Intrathecal Gene Therapy Onasemnogene Abeparvovec Phase III Study Meets Primary Endpoint in Children and Young Adults with SMA

December 30, 2024
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Novartis today announced positive topline results from the Phase III STEER study. This pivotal study assessed the efficacy and safety of investigational intrathecal onasemnogene abeparvovec […]

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