Research
Spring 2016 Issue of Compass Now Available
The Spring 2016 issue of Compass is now available online. As part of our most recent round of funding, we’ve announced eight grants totaling $890,000 […]
Cure SMA Awards $300,000 Drug Discovery Grant to Charlotte Sumner, in Collaboration with Imago Pharmaceuticals
Cure SMA has awarded a $300,000 drug discovery grant to Charlotte Sumner, MD, at Johns Hopkins University, in collaboration with Imago Pharmaceuticals. The award is […]
Cure SMA Releases Full Schedule for the 2016 Annual SMA Conference
Cure SMA has released the full schedule for the 2016 Annual SMA Conference, which will be held in Anaheim, CA at Disneyland, June 16-19. The […]
Cure SMA Awards $70,000 Grant to Christine DiDonato, Lurie Children’s Hospital of Chicago
Cure SMA has awarded a $70,000 research grant to Dr. Christine DiDonato at Lurie Children’s Hospital of Chicago for her project, “Assessing mediators of muscle […]
AveXis Reports Data from Ongoing Phase 1 Trial of AVXS-101 in Spinal Muscular Atrophy Type 1
Today, AveXis, Inc. presented an interim analysis of data as of April 1, 2016 from the ongoing Phase 1 trial of AVXS-101 for the treatment […]
Cure SMA Announces 2016 Family Friendly Poster Session Presenters
The Family Friendly Research Poster Session is one of the most anticipated events of our Annual SMA Conference. Each year, Cure SMA invites researchers from […]
Ionis Releases Data Update from Phase 2 Study in Infants with SMA
Ionis Pharmaceuticals provided an update on its ongoing open-label Phase 2 clinical study of nusinersen in infants with spinal muscular atrophy (SMA) at the American […]
Annual SMA Conference to Host Panels on NDA Process and SMA Drugs in Development
One of the most significant aspects of the Annual SMA Conference is the bringing together of families and researchers in the same event. The 2016 […]
Cure SMA-Funded Researchers Receive NIH Grant
Cure SMA-funded researcher Peter Schultz has been awarded a four-year NIH grant of just over $2 million to support his research into small molecules to […]
Cure SMA Awards $30,000 Grant to Jocelyn Cote, PhD, University of Ottawa
Cure SMA has awarded a $30,000 research grant to Jocelyn Cote, PhD, at the University of Ottawa for his project, “The role of SMN as […]