Research

Spinal Muscular Atrophy Mice Model Results Published in the Journal Science

August 26, 2014
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On August 7, the journal Science published results of a preclinical study demonstrating that treatment with orally available RNA splicing modifiers of the SMN2 gene […]

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Isis Begins Phase III Clinical Trial

August 25, 2014
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On August 1, Isis Pharmaceuticals, Inc. announced today the initiation of a pivotal Phase III study evaluating ISIS-SMNRx in infants with spinal muscular atrophy (SMA). […]

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Cure SMA Announces New Research Funding

August 25, 2014
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Cure SMA is proud to announce that we will be committing $1.8 million to new research funding over the next 12 months. Fifteen years ago, […]

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