Front Page News
Collaborative Ways Cure SMA is Driving Research Results
Much as families in our community often work together to start a chapter, organize an event, or raise awareness of SMA, researchers must work together […]
Meet the SMA Family that Helped Inspire 21st Century Cures
In a recent update on the 21st Century Cures Initiative, we shared how the SMA community has helped inspire this legistlation. Chairman Fred Upton has […]
Cytokinetics and Astellas Release Further Details on Upcoming Phase 2 Trial
Cytokinetics, in partnership with Astellas, has officially announced that recruitment will begin in the second half of 2015 for a Phase 2 clinical trial testing […]
Cure SMA Joins The Research Acceleration and Innovation Network
Cure SMA has become a participating organization of The Research Acceleration and Innovation Network (TRAIN), a program of FasterCures, bringing the total number of venture […]
Update on SMA-FDA Interactions
The SMA drug pipeline has grown dramatically in just over a decade. Of the 17 programs in the pipeline, seven of these are in clinical […]
2015 Family Friendly Poster Session Presenters Announced
The Family Friendly Research Poster Session is one of the most anticipated events of our Annual SMA Conference. Each year, Cure SMA invites researchers from […]
Update on Clinical Development of RG7800
F. Hoffman-La Roche, PTC and the SMA Foundation recently provided an update on the clinical development of RG7800, an investigational SMN2 splicing modifier that is […]
Cure SMA Funds $1.85 Million in New Research Grants in 2014-2015
Over the past few months, Cure SMA has announced a total of $1.85 million in new research funding. Our model is designed to fund both […]
Cure SMA Announces Additional $445,000 for Nationwide Children’s Hospital Gene Therapy Program led by Brian Kaspar, PhD
Cure SMA, the leading organization dedicated to the treatment and cure of spinal muscular atrophy (SMA), recently provided an additional $445,000 grant toward a gene […]
New 21st Century Cures Discussion Draft Released
The US House of Representatives Energy and Commerce Committee has released a new 21st Century Cures discussion draft. This is a revised and expanded version […]