Latest News
SMA Drug Pipeline Continues to Grow
This is an exciting time for the entire SMA community, as we celebrate another year of increasing momentum toward our goal of a treatment and cure for SMA. It’s also […]
Read More ›Cure SMA Researchers Present at Society for Neuroscience Meeting
The Society for Neuroscience (SfN) Meeting is the premiere neurobiology meeting, with over 30,000 scientists in attendance each year. This year’s meeting was held November 15-19 in Washington D.C. Two […]
Read More ›PTC Therapeutics Announces New Phase 1a/2b Clinical Trial
PTC Therapeutics, Inc. announced today that its joint development program in Spinal Muscular Atrophy (SMA) with Roche and the SMA Foundation (SMAF) has started a Phase 1b/2a study in adult […]
Read More ›Isis Announces Second Phase III Clinical Trial
Isis recently announced the start of CHERISH, a multi-center Phase III clinical study evaluating the efficacy and safety of the investigational compound, ISIS-SMNRx, in non-ambulatory children with Spinal Muscular Atrophy […]
Read More ›Southern California Gala of Hope Brings Community and Industry Partners Together to Raise $80,000
On November 15, 140 guests gathered for the Inaugural Southern California Cure SMA Gala of Hope. This fantastic evening raised over $80,000 in support of Cure SMA. Our thanks to […]
Read More ›Cure SMA Scientific Advisory Board Meets in Washington D.C.
Today and tomorrow, Cure SMA’s Scientific Advisory Board (SAB) will be meeting in Washington D.C. Our Scientific Advisory Board is a recognized group of experts in SMA and motor neuron […]
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