Dear SMA Community, We want to provide an update on Biogen’s efforts to help ensure the health and safety of the SMA community amid the novel Coronavirus (COVID-19). As you ...
As coronavirus, also known as COVID-19, continues to spread in communities, Cure SMA has also been closely tracking the situation. The health, safety, and well-being of the entire SMA community is important to ...
This article is part of a series of Cure SMA grant announcements being shared throughout the winter/spring. Cure SMA has awarded a $150,000 grant to Timra Gilson, Ph.D., of Indiana University, for her ...
This article is part of a series of Cure SMA grant announcements that will be shared throughout the next couple of months. Cure SMA has awarded a $150,000 grant to Dmytro Morderer, Ph.D., ...
This article is part of a series of Cure SMA grant announcements that will be shared throughout the next couple of months. Cure SMA has awarded a $170,000 research grant to Lyndsay Murray, ...
To help clinicians and the families they serve in the decision of when to administer therapy to infants identified with SMA via newborn screening, Cure SMA convened a working group comprised of 15 ...
This year, Rare Disease Day occurs on February 29—the rarest day of all! Spinal muscular atrophy (SMA) affects 12,000 people in the U.S. Yet, the SMA community is part of a greater community—the ...
Genentech, a member of the Roche Group, today presented 1-year data from the pivotal Part 2 of the SUNFISH study, evaluating risdiplam in people aged 2-25 years with Type 2 or Type 3 ...
Scholar Rock, a clinical-stage biopharmaceutical company focused on the treatment of serious diseases in which protein growth factors play a fundamental role, today highlighted key accomplishments of the past year and announced R&D ...
Elizabeth and Brian Veit live in Jefferson City, Mo., with their two children—Benjamin, who is 6 years old, and Kate, who is 5 years old. By all accounts, Elizabeth’s second pregnancy was “completely ...
