Now Available! New COVID-19 PPE Package from Cure SMA
As we continue to quarantine and see a new wave of COVID-19 cases across the country, Cure SMA would like you to know that our work for the spinal muscular atrophy (SMA) community ...
Results from Annual SMA Community Update Survey Now Published
Each year since 2017, Cure SMA has conducted a Community Update Survey. This online questionnaire is sent to all individuals with spinal muscular atrophy (SMA) and caregivers of children with SMA in the ...
Summit of Strength Virtual Webinar Series Continues Its Success!
A little more than six months ago, Cure SMA launched the Summit of Strength Virtual Webinar Series , a program designed to help support individuals and families with SMA manage the uncertainty of ...
NeurologyLive Article Now Available, Featuring an Interview with Cure SMA’s Dr. Mary Schroth
Through Cure SMA’s partnership with NeurologyLive, a new patient-centered article, “Early Intervention in SMA: How Access to Therapy Will Alter Disease Management As We Know It,” is now available for viewing ...
Cure SMA Publishes Paper in Partnership with NeurologyLive on Impact of COVID-19
Cure SMA has published a paper, titled “Spinal Muscular Atrophy and COVID-19: Guidance and Resources for Providers,” in partnership with NeurologyLive. The article highlights findings from a recent survey conducted by ...
Novartis Presents New Zolgensma® Data Further Demonstrating Therapeutic Benefit
Novartis Gene Therapies today announced new interim data from the ongoing Phase 3 STR1VE-EU clinical trial for Zolgensma® (onasemnogene abeparvovec). The data demonstrates that patients with spinal muscular atrophy (SMA) Type ...
Team Biogen Runs Over 22,000 Miles During SMA Awareness Month
Team Biogen hit the ground running throughout the month of August in honor of SMA Awareness Month. Together, the team logged 22,059 miles collectively from August 1st to August ...
Biogen Q3 2020 Community Statement: COVID-19 Updates and Latest Milestones
Dear Members of the SMA Community, We continue to work with the healthcare community to help people and families living with SMA get the support they need. As such, we wanted to share ...
Scholar Rock Announces that SRK-015 has Received Rare Pediatric Disease Designation from U.S. FDA for the Treatment of SMA
Scholar Rock, a clinical-stage biopharmaceutical company focused on the treatment of serious diseases in which protein growth factors play a fundamental role, today announced that the U.S. Food and Drug Administration (FDA) has ...
Genentech Releases Evrysdi™ FDA Approval Letter to the SMA Community
Dear SMA Patient Advocacy Community, As part of our ongoing partnership and following your request to receive updates about the risdiplam clinical development program, we are delighted to share with you a much-anticipated ...
Cure SMA Launches New Medical Alert Bracelet Support Program
Along with funding SMA research and care, Cure SMA provides thousands of individuals and families with vital support and resources that help people navigate life with spinal muscular atrophy (SMA). In addition to ...
Join Cure SMA for Our First-Ever Walk-n-Roll Virtual Celebration Ceremony
Cure SMA will host our first-ever Virtual Walk-n-Roll Celebration Ceremony on Saturday, May 30, 2020 at 11 a.m. EDT/10 a.m. CDT/9 a.m. MDT/8 a.m. PDT. Join us as we celebrate everything our community has achieved ...