Originally published on January 22, 2014. PTC announces that its SMA drug program, partnered with Roche, begins Phase I Safety Trials in healthy, adult volunteers. This brings the total number of SMA programs in clinical development to 5. PTC Therapeutics, the SMA Foundation, and Roche announced today that their joint research program in SMA has […]
Originally published on February 20, 2014. Cure SMA is proud to announce our new basic research funding for 2014. We are leading the way to a world without SMA by advancing a comprehensive research program, of which basic research is a key component. Basic research helps us understand what causes SMA, by revealing new and
Originally published on February 27, 2014. Cure SMA is leading the way to a world without SMA by advancing a comprehensive research program, of which basic research is a key component. Cure SMA has awarded 79 basic grants for a total of $9,507,612 in the past 10 years. Drs. Laurent and Lutz from Jackson Laboratory
Originally published on March 4, 2014. Cure SMA is leading the way to a world without SMA by advancing a comprehensive research program, of which basic research is a key component. Cure SMA has awarded 79 basic grants for a total of $9,507,612 in the past 10 years. Dr. Burnett of the Uniformed Services University
Originally published on March 6, 2014. A critical way Cure SMA advances research is by hosting and financially supporting The SMA Research Group Meeting. The meeting is the largest SMA research conference in the world. For 18 years, Cure SMA has hosted the conference with the goal of bringing the leading researchers from around the
Originally published on March 11, 2014. Cure SMA is leading the way to a world without SMA by advancing a comprehensive research program, of which basic research is a key component. Cure SMA has awarded 79 basic grants for a total of $9,507,612 in the past 10 years. Dr. Ebert at the Medical College of
Cure Spinal Muscular Atrophy Awards New Research Funding of $95,000 to Dr. Allison Ebert Read More »
Originally published on March 19, 2014. Cure SMA is leading the way to a world without SMA by advancing a comprehensive research program, of which basic research is a key component. Cure SMA has awarded 79 basic grants for a total of $9,507,612 in the past 10 years. Dr. Ke-Jun Han at the University of
Cure Spinal Muscular Atrophy Awards New Research Funding of $95,000 to Dr. Kejun Han Read More »
Originally published on March 25, 2014. Cure SMA is leading the way to a world without SMA by advancing a comprehensive research program, of which basic research is a key component. Cure SMA has awarded 79 basic grants for a total of $9,507,612 in the past 10 years. Dr. Rashmi Kothary at The Ottawa Hospital
Originally published on April 1, 2014. Cure SMA is leading the way to a world without SMA by advancing a comprehensive research program, of which basic research is a key component. Cure SMA has awarded 79 basic grants for a total of $9,507,612 in the past 10 years. Dr. Chien Ping Ko at The University
Cure Spinal Muscular Atrophy Awards New Research Funding of $75,000 to Dr. Chien-Ping Ko Read More »
Originally published on April 1, 2014. REGENX Biosciences, LLC and AveXis, Inc. announce that they have entered into an exclusive agreement for the development and commercialization of products to treat Spinal Muscular Atrophy (SMA) using NAV rAAV9 vectors. Under the terms of the agreement, REGENX granted AveXis an exclusive, worldwide license, with rights to sublicense,
